A Pioneer in Gene Therapy
The Powell Gene Therapy Center (PGTC) at the University of Florida has been instrumental in the development of newer, safer agents for the delivery of therapeutic genes to patients with genetic diseases, such as cystic fibrosis (CF) and alpha 1-antitrypsin deficiency (AAT-D).
manufacturing labs
Lab
Vector Core Lab
The Vector Core manufactures research-grade gene transfer vectors for use in pre-clinical investigations.
lab
Toxicology Core
The Toxicology Core is responsible for conducting animal and in vitro toxicology studies that the FDA determines are needed before a particular clinical gene transfer trial can begin.
gene therapy news
A beacon of hope
Barry Byrne, M.D., Ph.D., receives “See The Light” Award from the Mathew Forbes Romer Foundation
UF Health researchers working to develop COVID-19…
A team of University of Florida Health researchers is using an established gene therapy technique to quickly develop a COVID-19 vaccine that could…
What’s Holding Back Gene Therapy?
Gene therapy is finally poised to revolutionize the treatment of many diseases, but the nascent field is facing challenges — notably in…
