A Pioneer in Gene Therapy

The Powell Gene Therapy Center (PGTC) at the University of Florida has been instrumental in the development of newer, safer agents for the delivery of therapeutic genes to patients with genetic diseases, such as cystic fibrosis (CF) and alpha 1-antitrypsin deficiency (AAT-D).

manufacturing labs


Toxicology Core

The Toxicology Core is responsible for conducting animal and in vitro toxicology studies that the FDA determines are needed before a particular clinical gene transfer trial can begin.

Toxicology Core

gene therapy news

A beacon of hope

Category: News & Events

Barry Byrne, M.D., Ph.D., receives “See The Light” Award from the Mathew Forbes Romer Foundation

Kevin Romer, Barry Byrne, M.D., Ph.D., and David Ogman