A Pioneer in Gene Therapy

The Powell Gene Therapy Center (PGTC) at the University of Florida has been instrumental in the development of newer, safer agents for the delivery of therapeutic genes to patients with genetic diseases, such as cystic fibrosis (CF) and alpha 1-antitrypsin deficiency (AAT-D).

manufacturing labs

Lab

Vector Core Lab

The Vector Core manufactures research-grade gene transfer vectors for use in pre-clinical investigations.

Vector Core

lab

Human Applications Lab

The Human Applications Laboratory manufactures gene transfer vectors under cGMP for use in human clinical trials.

Human Applications

lab

Toxicology Core

The Toxicology Core is responsible for conducting animal and in vitro toxicology studies that the FDA determines are needed before a particular clinical gene transfer trial can begin.

Toxicology Core

lab

Process & Development Lab

The mission of the Process and Development Laboratory of PGTC (PD) is to develop methods for large-scale manufacturing of rAAV stocks in a GMP-translatable manner.

Process Development & Quality Control

gene therapy news

A beacon of hope

Category: News & Events

Barry Byrne, M.D., Ph.D., receives “See The Light” Award from the Mathew Forbes Romer Foundation

Kevin Romer, Barry Byrne, M.D., Ph.D., and David Ogman

Apic Bio Announces Formation of Scientific…

Category: News & Events

Apic Bio, Inc. today announced the formation of its Scientific Advisory Board (SAB) which includes internationally recognized gene therapy experts.

Byrne Headshot

UF Health researchers working to develop COVID-19…

Category: News & Events

A team of University of Florida Health researchers is using an established gene therapy technique to quickly develop a COVID-19 vaccine that could…

Group of scientist working in a lab