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Powell Gene Therapy Center Department of Pediatrics | College of Medicine
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About Overview
  • Our Team
  • Director
  • Our Mission
  • Pre-Clinical Research
  • Current Research
  • PGTC Labs
  • Collaborators

Current Research

Animal Models of Diseases

  • Transgenic Mice

Cancer

  • Targeted Liposomes as a Novel Delivery Method for Nucleic Acids
  • Drug Resistance of Normal Hematopoietic Stem Cells
  • Mechanisms of Radioprotection in Hematopoiesis

Cardiovascular Disease

  • Gene Therapy for Arterial Restenosis
  • Gene Therapy for Hypertension

CNS Applications

  • Central Nervous System Tramua
  • Parkinson’s
  • Alzheimers’s

Endocrine Diseases

  • Diabetes

Eye Diseases

  • Ocular Applications of Recombinant AAV
  • Experimental Optic Neuritis: Oxidative Injury
  • Reduction of Scarring Following Trabeculectomy using Transiently Transfected Ribozymes to TGF-b

Inflammatory Diseases

  • Gene Transfer as a Novel Means to Deliver Anti-cytokine Therapies in Sepsis/Trauma

Metabolic Disorders

  • PKU

Neuromuscular Disease

  • Gene Therapy for Pompe’s Disease

Pulmonary Disease

  • Alpha-1-antitrypsin Deficiency

 

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Powell Gene Therapy Center Department of Pediatrics | College of Medicine

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Physical Address
Academic Research Building
RG-130
Phone
(352) 294-5171
Email
pgtc-webinfo@peds.ufl.edu
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