Publications for Thomas J Conlon, PhD; Kirsten Coleman, and Kirsten Erger:
- Kondratov, O., Kondratova, L., Mandel, R. J., Coleman, K., Savage, M. A., Gray-Edwards, H. L., Ness, T. J., Rodriguez-Lebron, E., Bell, R. D., Rabinowitz, J., Gamlin, P. D., & Zolotukhin, S. (2021). A comprehensive study of a 29-capsid AAV library in a non-human primate central nervous system. Molecular therapy : the journal of the American Society of Gene Therapy, S1525-0016(21)00364-6. Advance online publication. https://doi.org/10.1016/j.ymthe.2021.07.010
- Hamm, S. E., Fathalikhani, D. D., Bukovec, K. E., Addington, A. K., Zhang, H., Perry, J. B., McMillan, R. P., Lawlor, M. W., Prom, M. J., Vanden Avond, M. A., Kumar, S. N., Coleman, K. E., Dupont, J. B., Mack, D. L., Brown, D. A., Morris, C. A., Gonzalez, J. P., & Grange, R. W. (2021). Voluntary wheel running complements microdystrophin gene therapy to improve muscle function in mdx mice. Molecular therapy. Methods & clinical development, 21, 144–160. https://doi.org/10.1016/j.omtm.2021.02.024
- Daniel, H. D., Kumar, S., Kannangai, R., Lakshmi, K. M., Agbandje-Mckenna, M., Coleman, K., Srivastava, A., Srivastava, A., & Abraham, A. M. (2021). Prevalence of Adeno-Associated Virus 3 Capsid Binding and Neutralizing Antibodies in Healthy and Hemophilia B Individuals from India. Human gene therapy, 32(9-10), 451–457. https://doi.org/10.1089/hum.2020.258
- Bolfer, L., Estrada, A. H., Larkin, C., Conlon, T. J., Lourenco, F., Taggart, K., Suzuki-Hatano, S., & Pacak, C. A. (2020). Functional Consequences of PDK4 Deficiency in Doberman Pinscher Fibroblasts. Scientific reports, 10(1), 3930. https://doi.org/10.1038/s41598-020-60879-6
- Byrne, B. J., Fuller, D. D., Smith, B. K., Clement, N., Coleman, K., Cleaver, B., Vaught, L., Falk, D. J., McCall, A., & Corti, M. (2019). Pompe disease gene therapy: neural manifestations require consideration of CNS directed therapy. Annals of translational medicine, 7(13), 290. https://doi.org/10.21037/atm.2019.05.56
- Mondo, E., Moser, R., Gao, G., Mueller, C., Sena-Esteves, M., Sapp, E., Pfister, E., O’Connell, D., Takle, K., Erger, K. E., Liu, W., Conlon, T. J., DiFiglia, M., Gounis, M. J., & Aronin, N. (2018). Selective Neuronal Uptake and Distribution of AAVrh8, AAV9, and AAVrh10 in Sheep After Intra-Striatal Administration. Journal of Huntington’s disease, 7(4), 309–319. https://doi.org/10.3233/JHD-180302
- Song, C., Conlon, T. J., Deng, W. T., Coleman, K. E., Zhu, P., Plummer, C., Mandapati, S., Van Hoosear, M., Green, K. B., Sonnentag, P., Sharma, A. K., Timmers, A., Robinson, P. M., Knop, D. R., Hauswirth, W. W., Chulay, J. D., Shearman, M. S., & Ye, G. J. (2018). Toxicology and Pharmacology of an AAV Vector Expressing Codon-Optimized RPGR in RPGR-Deficient Rd9 Mice. Human gene therapy. Clinical development, 29(4), 188–197. https://doi.org/10.1089/humc.2018.168
- Lee, Y. M., Conlon, T. J., Specht, A., Coleman, K. E., Brown, L. M., Estrella, A. M., Dambska, M., Dahlberg, K. R., & Weinstein, D. A. (2018). Long-term safety and efficacy of AAV gene therapy in the canine model of glycogen storage disease type Ia. Journal of inherited metabolic disease, 41(6), 977–984. https://doi.org/10.1007/s10545-018-0199-7
- Conlon, T. J., & Mavilio, F. (2018). The Pharmacology of Gene and Cell Therapy. Molecular therapy. Methods & clinical development, 8, 181–182. https://doi.org/10.1016/j.omtm.2017.12.007
- Corti, M., Liberati, C., Smith, B. K., Lawson, L. A., Tuna, I. S., Conlon, T. J., Coleman, K. E., Islam, S., Herzog, R. W., Fuller, D. D., Collins, S. W., & Byrne, B. J. (2017). Safety of Intradiaphragmatic Delivery of Adeno-Associated Virus-Mediated Alpha-Glucosidase (rAAV1-CMV-hGAA) Gene Therapy in Children Affected by Pompe Disease. Human gene therapy. Clinical development, 28(4), 208–218. https://doi.org/10.1089/humc.2017.146