Posted in

News & Events

Josh’s Fight to Cure FA

Please watch this video of Josh and donate whatever you can to help him and the thousands of people worldwide with FA (Friedreich’s ataxia), a debilitating, life-shortening, degenerative neuro-muscular disorder. We thank you from the bottom of our hearts! All you have to do is click on the following link to…

UF teams with company to advance gene therapy treatments

A biotechnology company has raised $30 million to advance gene therapy treatments developed at the University of Florida Powell Gene Therapy Center. The funding also will help UF Health researchers bring a novel form of gene therapy to patients with Pompe disease, a rare form of muscular dystrophy.